A Small Molecule That Targets r(CGG) exp and Improves Defects in Fragile X-Associated Tremor Ataxia Syndrome

Matthew Disney (1) , Biao Liu (1) , Wang-Yong Yang (1) , Chantal Sellier (2) , Tuan Tran (1, 3) , Nicolas Charlet-Berguerand (2) , Jessica Childs-Disney (2)

1 The Scripps Research Institute [La Jolla, San Diego]
2 IGBMC - Institut de Génétique et de Biologie Moléculaire et Cellulaire
3 SUNY Buffalo - University at Buffalo [SUNY]

Domaines: Sciences du Vivant [q-bio]

Matthew Disney, Biao Liu, Wang-Yong Yang, Chantal Sellier, Tuan Tran, et al.. A Small Molecule That Targets r(CGG) exp and Improves Defects in Fragile X-Associated Tremor Ataxia Syndrome. ACS Chemical Biology, 2012, 7 (10), pp.1711-1718. ⟨10.1021/cb300135h⟩. ⟨hal-03339570⟩