Management goals for type 1 Gaucher disease: An expert consensus document from the European working group on Gaucher disease

M. Biegstraaten , M. Cox , N. Belmatoug , M.G Berger (1) , T. Collin-Histed , S. Vom Dahl , M. Di Rocco (2) , C. Fraga , F. Giona , P. Giraldo , M. Hasanhodzic , A. Hughes (3) , P.O. Iversen , A. Kiewiet , E. Lukina , M. Machaczka , T. Marinakis , E. Mengel , M. Pastores , U. Plöckinger , H. Rosenbaum , C. Serratrice , A. Symeonidis , J. Szer , J. Timmerman , A. Tylki-Szymańska , M. Weisz Hubshman , D.I. Zafeiriou , A. Zimran , C.E.M. Hollak (4)

1 CHELTER - Role of intra-Clonal Heterogeneity and Leukemic environment in ThErapy Resistance of chronic leukemias
2 Department of Surgical Oncology
3 UKZN - University of KwaZulu-Natal [Durban, Afrique du Sud]
4 Department of Endocrinology and Metabolism

Domaines: Hématologie

M. Biegstraaten, M. Cox, N. Belmatoug, M.G Berger, T. Collin-Histed, et al.. Management goals for type 1 Gaucher disease: An expert consensus document from the European working group on Gaucher disease. Blood Cells, Molecules and Diseases, 2018, 68, pp.203 - 208. ⟨10.1016/j.bcmd.2016.10.008⟩. ⟨hal-01672894⟩