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, planned and performed most of the experiments. M.N. planned and performed the patch clamp measurements. L.F. helped with the iPSC differentiations and organized the schematic graph of MN differentiation. P.B. provided support for the electron microscopy experiments
, helped with the axonal transport measurements and P.V.B. wrote the axonal transport analysis software. M.J. provided ACY-738. T.T. and N.G. provided technical support, Jo.S. helped with the images and Ti.V. was involved in the ASO experiments. P.V.D. provided fibroblasts and ideas for the project, F.W. and S.P. supervised part of the iPSC differentiation and the patch clamp recordings of motor neurons, Ja. S contributed to the additional iPSC control lines in the patch clamp recordings