Immunogenicity Ectopic expression Eye surgery Immunomodulation GC-content Antibody responses Cone photoreceptors Assembly-activating protein Immunogenicity inflammation gene therapy AAV Human-monocyte-derived dendritic cells DMD Intra-cerebrospinal fluid injection Crigler–Najjar Syndrome Capsid Skeletal muscle Bioorthogonality Capsid assembly In vivo Congenital amaurosis Air tamponade Click chemistry Bioconjugates Engineering Exon skipping Homopolymers Homogeneity AAV AAP Dynamin 2 Humoral immunity Gene Therapy Inherited retinal dystrophies Centronuclear myopathy Gait assessment Cell therapy CNS Baculovirus expression vector Homologous recombination Inflammation GRMD Gene transfer High-throughput technology Immune responses Exercise Gene-therapy Accelerometry Intravitreal Antibodies/immunology/metabolism Childhood blindness Discriminant analysis Capsid thermal stability Intrathymic gene transfer DMDmdx rat Manufacturing Insect cells Dystrophin Immune response Clinical trial Animal model Age Impurities Dose study Acute treatment High-throughput sequencing Analytical ultracentrifugation Baculovirus Capsid thermostability Treg Mice Infectivity Adeno-associated virus CMC AAV vectors Vector Clinical trials Genes Cerebellum Adenoviridae/immunology Fluid-air exchange AAV vector Duchenne muscular dystrophy Cell–virus interaction Identity Duchenne Gene therapy CD8 + T lymphocytes GRMD dog Identity assay ABCA4 Calcium Beta-subunit Adenoassociated viral vector Animals Tolerance Gene Transfer Immunosuppression B-Lymphocytes/immunology/metabolism AUC Quality control Innate immunity